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Tag: Rare Diseases
Health & Lifestyle
Roche Initiates New Elevidys Study After EU Regulator F...
Roche has launched a new Elevidys study following feedback from European regulat...
Health & Lifestyle
Scientists Identify New Rare Genetic Disease Using Whol...
Scientists have identified a new rare genetic disease using whole-exome sequenci...
Health & Lifestyle
Soleno Withdraws EU Rare Disease Drug Application Ahead...
Soleno Therapeutics has withdrawn its EU application for a rare disease drug ahe...
Health & Lifestyle
Neurocrine Nears $2.5 Billion Deal to Acquire Soleno Th...
Neurocrine Biosciences is nearing a $2.5 billion deal to acquire Soleno Therapeu...
Health & Lifestyle
Biogen to Acquire Apellis Pharmaceuticals for $5.6 Bill...
Biogen will acquire Apellis Pharmaceuticals for $5.6 billion as part of its stra...
Health & Lifestyle
US FDA Warns of Liver Injury Risk Linked to Amgen’s Rar...
The US FDA has issued a warning بشأن potential liver injury cases associated wit...
Health & Lifestyle
US FDA Lifts Partial Clinical Hold on Rezolute’s Low Bl...
The US FDA has lifted a partial clinical hold on Rezolute’s low blood sugar trea...
Health & Lifestyle
Purdue University Advances Rare Disease Drug Discovery ...
Purdue University is accelerating rare disease drug discovery using the WELLJET ...
Health & Lifestyle
GSK’s Linerixibat Receives US FDA Approval for Treatmen...
GSK has received US FDA approval for linerixibat, a treatment for a rare liver d...
Health & Lifestyle
US FDA Approves Denali Therapeutics’ Genetic Disorder T...
The US FDA has approved Denali Therapeutics’ treatment for a rare genetic disord...